/wp-content/uploads/4dmt_logo.svg00Maria Gonzalez/wp-content/uploads/4dmt_logo.svgMaria Gonzalez2023-03-13 16:43:562023-03-13 16:48:36In Vitro Fabry Disease Correction in Patient iPSC-Derived Cardiomyocytes and Endothelial Cells Using an Evolved and Optimized AAV Gene Therapeutic (4D-310)
/wp-content/uploads/4dmt_logo.svg00Maria Gonzalez/wp-content/uploads/4dmt_logo.svgMaria Gonzalez2023-03-13 16:34:582023-03-13 16:41:53Highly-Evolved Novel AAV Gene Therapy Directly Addresses Fabry Disease Pathology In Vivo by Cell Autonomous Expression in the Heart and Other Target Organs
/wp-content/uploads/4dmt_logo.svg00Maria Gonzalez/wp-content/uploads/4dmt_logo.svgMaria Gonzalez2023-03-13 13:00:552023-03-13 17:09:404D-C102, a Novel Muscle-Tropic AAV Variant Demonstrates Superior Gene Delivery in Cardiac and Skeletal Muscle Tissues Versus Wild-Type AAV in Human Cells and Non-Human Primates